1. Department of Pediatrics; University of Rome Tor Vergata and Bambino Gesù Children's Hospital; Rome Italy
2. Department of Medical Genetics; Bambino Gesù Children's Hospital; Rome Italy
3. San Raffaele Telethon Institute for Gene Therapy (TIGET); Division of Regenerative Medicine, Stem Cells, and Gene Therapy; IRCCS San Raffaele Scientific Institute; Milan Italy
4. Pediatric Immunohematology and Bone Marrow Transplantation Unit; IRCCS San Raffaele Scientific Institute; Milan Italy
5. Vita-Salute San Raffaele University; Milan Italy