Eradication of factor IX neutralizing and anaphylactic inhibitors in a patient with severe haemophilia B using cyclophosphamide immune suppression and factor IX desensitization
Author:
Affiliation:
1. University of North Dakota School of Medicine and Health Sciences Grand Forks ND USA
2. Sanford Medical Center Fargo Fargo ND USA
3. Roger Maris Cancer Center Sanford Health Fargo ND USA
Publisher
Wiley
Subject
Genetics (clinical),Hematology,General Medicine
Link
https://onlinelibrary.wiley.com/doi/pdf/10.1111/hae.13926
Reference10 articles.
1. Inhibitor development in haemophilia B: an orphan disease in need of attention
2. Hemophilia B: molecular pathogenesis and mutation analysis
3. Immunosuppressive agents in the treatment of inhibitors in congenital haemophilia A and B - a systematic literature review
4. Nephrotic Syndrome as a Complication of Immune Tolerance in Hemophilia B
5. Ablation of hemophilic FVIII inhibitors with FVIII priming, cyclophosphamide immune suppression, and rapid tapering of FVIII immune tolerance
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1. Factor IX antibodies and tolerance in hemophilia B in the Nordic countries – The impact of F9 variants and complications;Thrombosis Research;2022-09
2. Immune tolerance induction using Fc‐fusion‐protein recombinant factor IX in severe haemophilia B;Haemophilia;2021-10-02
3. Nonacog-α;Reactions Weekly;2020-04
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