Efficacy, safety and bioequivalence of the human‐derived B‐domain‐deleted recombinant factor VIII TQG202 for prophylaxis in severe haemophilia A patients

Author:

Xi Yaming1,Jin Chenghao2,Liu Wei3,Zhou Hu4,Wang Zhen5,Zhou Rongfu6,Lou Shifeng7,Zhao Xielan8,Chen Fangping8,Cheng Peng9,Sun Zimin10,Jia Haifei11,Zhang Lei3

Affiliation:

1. Department of Hematology The First Hospital of Lanzhou University Lanzhou, Gansu Province China

2. Hemophilia Information Management Center of Jiangxi Province Jiangxi Provincial People's Hospital Nanchang China

3. State Key Laboratory of Experimental Hematology, National Clinical Research Center for Blood Diseases, Haihe Laboratory of Cell Ecosystem, Institute of Hematology & Blood Diseases Hospital,Tianjin Key Laboratory of Gene Therapy for Blood Diseases, CAMS Key Laboratory of Gene Therapy for Blood Diseases Institute of Hematology & Blood Diseases Hospital Chinese Academy of Medical Sciences & Peking Union Medical College Tianjin China

4. Department of Hematology The Cancer Hospital affiliated to Zhengzhou University Zhengzhou China

5. Department of Hematology Henan Provincial People's Hospital People's Hospital of Zhengzhou University Zhengzhou China

6. Department of Hematology Affiliated Drum Tower Hospital Medical School of Nanjing University Nanjing Jiangsu China

7. Department of Hematology The Second Affiliated Hospital Chongqing Medical University Chongqing China

8. Department of Hematology Xiangya Hemophilia Diagnosis and Treatment Center Xiangya Hospital Central South University Changsha Hunan Province China

9. Department of Hematology The First Affiliated Hospital of Guangxi Medical University Nanning Guangxi Province China

10. Department of Hematology The Affiliated Provincial Hospital of Anhui Medical University Hefei China

11. R&D Institute Chia Tai Tianqing Pharmaceutical Group Co. Ltd. Nanjing Jiangsu Province China

Publisher

Wiley

Subject

Genetics (clinical),Hematology,General Medicine

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