Treatment of β654-thalassaemia by TALENs in a mouse model-Reference-Cited by-同舟云学术

Treatment of β654-thalassaemia by TALENs in a mouse model

Published:2018-08-02 Issue:6 Volume:51 Page:e12491
ISSN:0960-7722
Container-title:Cell Proliferation
language:en
Short-container-title:Cell Prolif

Author:

Fang Yudan¹²³,Cheng Yan¹²³⁴,Lu Dan¹³,Gong Xiuli¹³,Yang Guanheng¹³,Gong Zhijuan¹³,Zhu Yiwen¹³,Sang Xiao¹³,Fan Shuyue²⁴,Zhang Jingzhi¹³,Zeng Fanyi¹²³⁴^ORCID

Affiliation:

1. Shanghai Children's Hospital; Shanghai Institute of Medical Genetics; Shanghai Jiao Tong University; Shanghai China

2. Department of Histo-Embryology, Genetics and Developmental Biology; Shanghai Jiao Tong University School of Medicine; Shanghai China

3. Key Laboratory of Embryo Molecular Biology; Ministry of Health & Shanghai Key Laboratory of Embryo and Reproduction Engineering; Shanghai China

4. Institute of Medical Science; Shanghai Jiao Tong University School of Medicine; Shanghai China

Funder

National Basic Research Program of China

National Natural Science Foundation of China

Natural Science Foundation of Shanghai

Shanghai Municipal Commission of Health and Family Planning Grant

Experimental Animals Project of Shanghai Municipality

Shanghai Sailing Program

Project of Academician Workstation at KingMed Diagnostics

Publisher

Wiley

Subject

Cell Biology,General Medicine

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1111/cpr.12491/fullpdf

Reference36 articles.

1. Global epidemiology of haemoglobin disorders and derived service indicators;Modell;Bull World Health Organ,2008

2. Survival in medically treatedpatients with homozygous beta-thalassemia;Olivieri;N Engl J Med,1994

3. Recent Progress on Genetic Diagnosis and Therapy for β-Thalassemia in China and Around the World;Zhang;Hum Gene Ther,2018

4. Detection of beta-thalassemia mutations in the Chinese using amplified DNA from dried blood specimens;Huang;Hum Genet,1990

5. RNA transcripts of the beta-thalassaemia allele IVS-2-654 C->T: a small amount of normally processed beta-globin mRNA is still produced from the mutant gene;Huang;Br J Haematol,1994

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