Therapy for β-globinopathies: a brief review and determinants for successful and safe correction
Author:
Publisher
Wiley
Subject
History and Philosophy of Science,General Biochemistry, Genetics and Molecular Biology,General Neuroscience
Link
http://onlinelibrary.wiley.com/wol1/doi/10.1111/j.1749-6632.2010.05584.x/fullpdf
Reference39 articles.
1. The cost of health care for children and adults with sickle cell disease;Kauf;Am. J. Hematol.,2009
2. Gene therapy for immunodeficiency due to adenosine deaminase deficiency;Aiuti;N. Engl. J. Med.,2009
3. LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1;Hacein-Bey-Abina;Science (New York, N.Y.),2003
4. Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1;Hacein-Bey-Abina;J. Clin. Invest.,2008
5. Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector;Gaspar;Lancet,2004
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