Research in haemophilia B - approaching the request for high evidence levels in a rare disease-Reference-Cited by-同舟云学术

Research in haemophilia B - approaching the request for high evidence levels in a rare disease

Published:2014-12-11 Issue:1 Volume:21 Page:4-20
ISSN:1351-8216
Container-title:Haemophilia
language:en
Short-container-title:Haemophilia

Author:

Berger K.¹,Schopohl D.¹,Hilger A.²,Behr Gross M. -E.³,Giangrande P.⁴,Peyvandi F.⁵,Seitz R.²,Schramm W.⁶

Affiliation:

1. Department of Haematology/Oncology; University Hospital of Munich; Munich Germany

2. Paul-Ehrlich-Institute; Langen Germany

3. European Directorate for the Quality of Medicines & HealthCare (EDQM); Council of Europe; Strasbourg France

4. Oxford Haemophilia & Thrombosis Centre; Oxford University Hospitals NHS Trust; Oxford Oxfordshire UK

5. Department of Pathophysiology and Transplantation; Angelo Bianchi Bonomi Haemophilia and Thrombosis Center; Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico; Università degli Studi di Milano; Luigi Villa Foundation; Milan Italy

6. Rudolf-Marx-Foundation; University of Munich; Munich Germany

Funder

Rudolf-Marx-Stiftung

Publisher

Wiley

Subject

Genetics (clinical),Hematology,General Medicine

Link

http://onlinelibrary.wiley.com/wol1/doi/10.1111/hae.12603/fullpdf

Reference48 articles.

1. Haemophilia B: impact on patients and economic burden of disease;Gater;Thromb Haemost,2011

2. Enhanced pharmacokinetic properties of a glycoPEGylated recombinant factor IX: a first human dose trial in patients with hemophilia B;Negrier;Blood,2011

3. Safety and pharmacokinetics of a novel recombinant fusion protein linking coagulation factor IX with albumin (rIX-FP) in hemophilia B patients;Santagostino;Blood,2012

4. Recombinant factor IX-Fc fusion protein (rFIXFc) demonstrates safety and prolonged activity in a phase 1/2a study in hemophilia B patients;Shapiro;Blood,2012

5. Present and future challanges in the treatment of haemophilia: a clinician's perspective;Mannucci;Blood Transfus,2013

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1. Single centre, real‐world experience of perioperative rFIXFc use in adult patients with haemophilia B undergoing major and minor surgery;Haemophilia;2021-10-06

2. Once‐weekly prophylactic treatment vs. on‐demand treatment with nonacog alfa in patients with moderately severe to severe haemophilia B;Haemophilia;2016-01-29