A Phase I/II Clinical Trial of β-Globin Gene Therapy for β-Thalassemia
Author:
Publisher
Wiley
Subject
History and Philosophy of Science,General Biochemistry, Genetics and Molecular Biology,General Neuroscience
Link
http://onlinelibrary.wiley.com/wol1/doi/10.1196/annals.1345.007/fullpdf
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4. Generation of a high-titer retroviral vector capable of expressing high levels of the human β-globin gene;Sadelain;Proc. Natl. Acad. Sci. USA,1995
5. Successful incorporation of extended LCR and β globin gene constructs in oncoretroviral and lentiviral vectors;Alkan;Mol. Ther.,2000
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