Home infusion program with enzyme replacement therapy for Fabry disease: The experience of a large Italian collaborative group-Reference-Cited by-同舟云学术

Home infusion program with enzyme replacement therapy for Fabry disease: The experience of a large Italian collaborative group

Published:2017-09 Issue: Volume:12 Page:85-91
ISSN:2214-4269
Container-title:Molecular Genetics and Metabolism Reports
language:en
Short-container-title:Molecular Genetics and Metabolism Reports

Author:

Concolino D.^ORCID,Amico L.,Cappellini M.D.,Cassinerio E.,Conti M.,Donati M.A.,Falvo F.,Fiumara A.,Maccarone M.,Manna R.,Matucci A.,Musumeci M.B.,Nicoletti A.,Nisticò R.,Papadia F.,Parini R.,Peluso D.,Pensabene L.,Pisani A.,Pistone G.,Rigoldi M.,Romani I.,Tenuta M.,Torti G.,Veroux M.,Zachara E.

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology

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4. Natural history of Fabry disease in females in the Fabry outcome survey;Deegan;J. Med. Genet.,2006

5. The relationship of vascular glycolipid storage to clinical manifestations of Fabry disease: a cross-sectional study of a large cohort of clinically affected heterozygous women;Gupta;Medicine (Baltimore),2005

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