Timing is everything: Clinical courses of Hunter syndrome associated with age at initiation of therapy in a sibling pair-Reference-Cited by-同舟云学术

Timing is everything: Clinical courses of Hunter syndrome associated with age at initiation of therapy in a sibling pair

Published:2022-03 Issue: Volume:30 Page:100845
ISSN:2214-4269
Container-title:Molecular Genetics and Metabolism Reports
language:en
Short-container-title:Molecular Genetics and Metabolism Reports

Author:

Grant Nathan,Sohn Young Bae,Ellinwood N. Matthew,Okenfuss Ericka,Mendelsohn Bryce A.,Lynch Leslie E.,Braunlin Elizabeth A.,Harmatz Paul R.,Eisengart Julie B.

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology

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4. Developmental and behavioral aspects of mucopolysaccharidoses with brain manifestations—neurological signs and symptoms;Shapiro;Mol. Genet. Metabolism,2017

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