Author:
Kelly Nicole R.,Orsini Joseph J.,Goldenberg Aaron J.,Mulrooney Niamh S.,Boychuk Natalie A.,Clarke Megan J.,Paleologos Katrina,Martin Monica M.,McNeight Hannah,Caggana Michele,Bailey Sean M.,Eiland Lisa R.,Ganesh Jaya,Kupchik Gabriel,Lumba Rishi,Nafday Suhas,Stroustrup Annemarie,Gelb Michael H.,Wasserstein Melissa P.
Funder
Takeda Pharmaceuticals USA Inc
BioMarin Pharmaceutical Inc
National Institute of Child Health and Human Development
Abeona Therapeutics Inc
Alexion Pharmaceuticals Inc
Ultragenyx Pharmaceutical Inc
Genzyme Corporation
Ara Parseghian Medical Research Fund
Subject
Endocrinology,Genetics,Molecular Biology