Classic and Atypical Late Infantile Neuronal Ceroid Lipofuscinosis in Latin America: Clinical and Genetic Aspects, and Treatment Outcome with Cerliponase Alfa-Reference-Cited by-同舟云学术

Classic and Atypical Late Infantile Neuronal Ceroid Lipofuscinosis in Latin America: Clinical and Genetic Aspects, and Treatment Outcome with Cerliponase Alfa

Published:2024-03 Issue: Volume:38 Page:101060
ISSN:2214-4269
Container-title:Molecular Genetics and Metabolism Reports
language:en
Short-container-title:Molecular Genetics and Metabolism Reports

Author:

Guelbert Norberto,Espitia Segura Oscar Mauricio,Amoretti Carolina,Arteaga Arteaga Angélica,Atanacio Nora Graciela,Bazan Natacha Sabrina,Carvalho Ellaine Doris Fernandes,Carvalho de Andrade Maria Denise Fernandes,Denzler Inés María,Durand Consuelo,Ribeiro Erlane,Giugni Juan Carlos,González Gabriel,González Moron Dolores,Guelbert Guillermo,Hernández Rodriguez Zulma Janneth,Embiruçu Emilia Katiane,Kauffman Marcelo Andrés,Mancilla Nury Isabel,Marcon Laureano,Marques Pereira Alessandra,Fischinger Moura de Souza Carolina,Muñoz Victor Adrián,Naranjo Flórez Ricardo Andrés,Pessoa André Luiz,Ruiz María Victoria,Solano Villareal Martha Luz,Spécola Norma,Tavera Lina Marcela,Tello Javiera,Troncoso Schifferli Mónica,Ugrina Sonia,Vaccarezza María Magdalena,Vergara Diane,Villanueva María Mercedes

Funder

BioMarin Pharmaceutical Inc

Publisher

Elsevier BV

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