Muscle imaging data in late-onset Pompe disease reveal a correlation between the pre-existing degree of lipomatous muscle alterations and the efficacy of long-term enzyme replacement therapy-Reference-Cited by-同舟云学术

Muscle imaging data in late-onset Pompe disease reveal a correlation between the pre-existing degree of lipomatous muscle alterations and the efficacy of long-term enzyme replacement therapy

Published:2015-06 Issue: Volume:3 Page:58-64
ISSN:2214-4269
Container-title:Molecular Genetics and Metabolism Reports
language:en
Short-container-title:Molecular Genetics and Metabolism Reports

Author:

Gruhn Kai Michael,Heyer Christoph Malte,Güttsches Anne-Katrin,Rehmann Robert,Nicolas Volkmar,Schmidt-Wilcke Tobias,Tegenthoff Martin,Vorgerd Matthias,Kley Rudolf Andre

Funder

Genzyme

Publisher

Elsevier BV

Subject

Endocrinology,Genetics,Molecular Biology

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4. Rate of progression and predictive factors for pulmonary outcome in children and adults with Pompe disease;van der Beek;Mol. Genet. Metab.,2011

5. Rapid progressive course of later-onset Pompe disease in Chinese patients;Yang;Mol. Genet. Metab.,2011

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