Gene therapy review: Duchenne muscular dystrophy case study
Author:
Publisher
Elsevier BV
Subject
Neurology (clinical),Neurology
Reference82 articles.
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1. Mechanisms of Chimeric Cell Therapy in Duchenne Muscular Dystrophy;Biomedicines;2024-09-02
2. Efficacy and safety of different doses of vamorolone in boys with Duchenne muscular dystrophy: a systematic review and network meta-analysis;Frontiers in Neurology;2024-08-21
3. Engineered mRNA Delivery Systems for Biomedical Applications;Advanced Materials;2023-10-08
4. Progress in hereditary neuropathies, myopathies and motoneuron disorders!;Revue Neurologique;2023-01
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