Pharmacokinetics and pharmacodynamics of PEGylated truncated human cystathionine beta-synthase for treatment of homocystinuria

Author:

Majtan TomasORCID,Bublil Erez M.,Park Insun,Arning Erland,Bottiglieri Teodoro,Glavin Frank,Kraus Jan P.

Funder

American Heart Association

Orphan Technologies Ltd.

Publisher

Elsevier BV

Subject

General Pharmacology, Toxicology and Pharmaceutics,General Biochemistry, Genetics and Molecular Biology,General Medicine

Reference36 articles.

1. Specific gravity of whole blood in Cynomolgus monkeys (Macaca fascicularis), squirrel monkeys (Saimiri sciureus), and tamarins (Saguinus labiatus) and total blood volume in Cynomolgus monkeys;Ageyama;Contemp. Top. Lab. Anim. Sci.,2001

2. Serum betaine, N,N-dimethylglycine and N-methylglycine levels in patients with cobalamin and folate deficiency and related inborn errors of metabolism;Allen;Metabolism,1993

3. Quantitation of S-Adenosylmethionine and S-Adenosylhomocysteine in plasma using liquid chromatography–electrospray tandem mass spectrometry;Arning;Methods Mol. Biol.,2016

4. Enzyme replacement with PEGylated cystathionine beta-synthase ameliorates homocystinuria in murine model;Bublil;J. Clin. Invest.,2016

5. Home infusion therapy is safe and enhances compliance in patients with mucopolysaccharidoses;Burton;Mol. Genet. Metab.,2009

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