Orphan Drugs and Their Impact on Pharmaceutical Development

Author:

Attwood Misty M.,Rask-Andersen Mathias,Schiöth Helgi B.

Funder

Swedish Society for Medical Research

Swedish Brain Foundation

Publisher

Elsevier BV

Subject

Pharmacology,Toxicology

Reference67 articles.

1. Developing products for rare diseases & conditions. [Online];U.S. Food and Drug Administration,2017

2. National Organization for Rare Disorders. [Online];National Organization for Rare Disorders (NORD),2017

3. RARE diseases: facts and statistics. [Online];Global Genes Organisation,2012

4. Profile of rare diseases;Institute of Medicine (US),2010

5. FAQs about rare diseases. [Online];Genetic and Rare Diseases Information Center (GARD),2017

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