N1303K: Leaving no stone unturned in the search for transformational therapeutics
Author:
Publisher
Elsevier BV
Subject
Pulmonary and Respiratory Medicine,Pediatrics, Perinatology and Child Health
Reference20 articles.
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2. Beyond Kaftrio : mechanistic insights to maximize N1303K-CFTR rescue;2024-03-03
3. Response to Elexacaftor/Tezacaftor/Ivacaftor in people with cystic fibrosis with the N1303K mutation: Case report and review of the literature;Heliyon;2024-03
4. Theratyping cystic fibrosis patients to guide elexacaftor/tezacaftor/ivacaftor out-of-label prescription;European Respiratory Journal;2023-09-11
5. Response to Elexacaftor/Tezacaftor/Ivacaftor in People with Cystic Fibrosis with the N1303k Mutation Case Report, and Review of the Literature;2023
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