Inhaled mRNA therapy for treatment of cystic fibrosis: Interim results of a randomized, double‐blind, placebo‐controlled phase 1/2 clinical study-Reference-Cited by-同舟云学术

Inhaled mRNA therapy for treatment of cystic fibrosis: Interim results of a randomized, double‐blind, placebo‐controlled phase 1/2 clinical study

Published:2023-07 Issue:4 Volume:22 Page:656-664
ISSN:1569-1993
Container-title:Journal of Cystic Fibrosis
language:en
Short-container-title:Journal of Cystic Fibrosis

Author:

Rowe S.M.^ORCID,Zuckerman J.B.^ORCID,Dorgan D.^ORCID,Lascano J.,McCoy K.^ORCID,Jain M.^ORCID,Schechter M.S.^ORCID,Lommatzsch S.,Indihar V.^ORCID,Lechtzin N.,McBennett K.,Callison C.,Brown C.^ORCID,Liou T.G.,MacDonald K.D.,Nasr S.Z.,Bodie S.^ORCID,Vaughn M.,Meltzer E.B.,Barbier A.J.

Funder

Cystic Fibrosis Foundation

National Institutes of Health

Publisher

Elsevier BV

Subject

Pulmonary and Respiratory Medicine,Pediatrics, Perinatology and Child Health

Reference31 articles.

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3. Cystic fibrosis patients of minority race and ethnicity less likely eligible for CFTR modulators based on CFTR genotype;McGarry;Pediatr Pulmonol,2021

4. Cystic fibrosis: emergence of highly effective targeted therapeutics and potential clinical implications;Mall;Am J Respir Crit Care Med,2020

5. Lipid nanoparticles for mRNA delivery;Hou;Nat Rev Mater,2021

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