1. Cystic fibrosis;Elborn;Lancet,2016
2. Rate of Uptake of Ivacaftor Use after U.S. Food and Drug Administration Approval among Patients Enrolled in the U.S. Cystic Fibrosis Foundation Patient Registry. Annals of the;Sawicki;Am Thorac Soc,2015
3. The impact of FDA and EMA regulatory decision-making process on the access to CFTR modulators for the treatment of cystic fibrosis;Costa;Orphanet J Rare Dis,2022
4. Cystic Fibrosis Foundation. Cystic Fibrosis Foundation Patient Registry 2022 Annual Data Report. Bethesda, MD: 2023.
5. Worldwide rates of diagnosis and effective treatment for cystic fibrosis;Guo;J Cyst Fibros,2022