Functional rescue of c.3846G>A (W1282X) in patient-derived nasal cultures achieved by inhibition of nonsense mediated decay and protein modulators with complementary mechanisms of action-Reference-Cited by-同舟云学术

Functional rescue of c.3846G>A (W1282X) in patient-derived nasal cultures achieved by inhibition of nonsense mediated decay and protein modulators with complementary mechanisms of action

Published:2020-09 Issue:5 Volume:19 Page:717-727
ISSN:1569-1993
Container-title:Journal of Cystic Fibrosis
language:en
Short-container-title:Journal of Cystic Fibrosis

Author:

Laselva Onofrio^ORCID,Eckford Paul DW,Bartlett Claire,Ouyang Hong,Gunawardena Tarini NA,Gonska Tanja,Moraes Theo J,Bear Christine E^ORCID

Publisher

Elsevier BV

Subject

Pulmonary and Respiratory Medicine,Pediatrics, Perinatology and Child Health

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