Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study-Reference-Cited by-同舟云学术

Nusinersen initiated in infants during the presymptomatic stage of spinal muscular atrophy: Interim efficacy and safety results from the Phase 2 NURTURE study

Published:2019-11 Issue:11 Volume:29 Page:842-856
ISSN:0960-8966
Container-title:Neuromuscular Disorders
language:en
Short-container-title:Neuromuscular Disorders

Author:

De Vivo Darryl C.,Bertini Enrico,Swoboda Kathryn J.,Hwu Wuh-Liang,Crawford Thomas O.,Finkel Richard S.,Kirschner Janbernd,Kuntz Nancy L.,Parsons Julie A.,Ryan Monique M.,Butterfield Russell J.,Topaloglu Haluk,Ben-Omran Tawfeg,Sansone Valeria A.,Jong Yuh-Jyh,Shu Francy,Staropoli John F.,Kerr Douglas,Sandrock Alfred W.,Stebbins Christopher,Petrillo Marco,Braley Gabriel,Johnson Kristina,Foster Richard,Gheuens Sarah,Bhan Ishir,Reyna Sandra P.,Fradette Stephanie,Farwell Wildon

Funder

Biogen

Publisher

Elsevier BV

Subject

Genetics (clinical),Neurology (clinical),Neurology,Pediatrics, Perinatology and Child Health

Reference45 articles.

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