In vivo delivery of naked antisense oligos in aged mdx mice: Analysis of dystrophin restoration in skeletal and cardiac muscle-Reference-Cited by-同舟云学术

In vivo delivery of naked antisense oligos in aged mdx mice: Analysis of dystrophin restoration in skeletal and cardiac muscle

Published:2008-08 Issue:8 Volume:18 Page:597-605
ISSN:0960-8966
Container-title:Neuromuscular Disorders
language:en
Short-container-title:Neuromuscular Disorders

Author:

Vitiello Libero,Bassi Nicola,Campagnolo Paola,Zaccariotto Eva,Occhi Gianluca,Malerba Alberto,Pigozzo Sarah,Reggiani Carlo,Ausoni Simonetta,Zaglia Tania,Gamba Piergiorgio,Baroni Maurizio D.,Ditadi Andrea P.

Publisher

Elsevier BV

Subject

Genetics (clinical),Neurology (clinical),Neurology,Pediatrics, Perinatology and Child Health

Reference24 articles.

1. Duchenne muscular dystrophy gene therapy: progress and prospects;Foster;Gene Ther,2006

2. Gene therapy: the “pro-sense” approach to Duchenne muscular dystrophy;van Deutekom;Eur J Hum Genet,2005

3. Splicing intervention for Duchenne muscular dystrophy;McClorey;Curr Opin Pharmacol,2005

4. Antisense-induced multiexon skipping for Duchenne muscular dystrophy makes more sense;Aartsma-Rus;Am J Hum Genet,2004

5. Multiexon skipping leading to an artificial DMD protein lacking amino acids from exons 45 through 55 could rescue up to 63% of patients with Duchenne muscular dystrophy;Beroud;Hum Mutat,2007

Cited by 29 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Upregulation of utrophin improves the phenotype of Duchenne muscular dystrophy hiPSC-derived CMs;Molecular Therapy - Nucleic Acids;2024-09

2. Morpholino oligonucleotide-mediated exon skipping for DMD treatment: Past insights, present challenges and future perspectives;Journal of Biosciences;2023-10-11

3. Multiomic characterization of disease progression in mice lacking dystrophin;PLOS ONE;2023-03-31

4. Using a State-of-the-Art Toolbox to Evaluate Molecular and Functional Readouts of Antisense Oligonucleotide-Induced Exon Skipping in mdx Mice;Nucleic Acid Therapeutics;2020-02-01

5. Restoration of Functional Full-Length Dystrophin After Intramuscular Transplantation of Foamy Virus-Transduced Myoblasts;Human Gene Therapy;2020-02-01