Author:
Weihl Conrad C.,Baloh Robert H.,Lee Youjin,Chou Tsui-Fen,Pittman Sara K.,Lopate Glenn,Allred Peggy,Jockel-Balsarotti Jennifer,Pestronk Alan,Harms Matthew B.
Funder
Ultragenyx Pharmaceuticals, Novato CA
NIH
Muscular Dystrophy Association
Myositis Association
Hope Center for Neurological Disorders
Burroughs Wellcome Fund
Subject
Genetics(clinical),Clinical Neurology,Neurology,Pediatrics, Perinatology, and Child Health
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