Measuring clinical effectiveness of medicinal products for the treatment of Duchenne muscular dystrophy-Reference-Cited by-同舟云学术

Measuring clinical effectiveness of medicinal products for the treatment of Duchenne muscular dystrophy

Published:2015-01 Issue:1 Volume:25 Page:96-105
ISSN:0960-8966
Container-title:Neuromuscular Disorders
language:en
Short-container-title:Neuromuscular Disorders

Author:

Lynn Stephen,Aartsma-Rus Annemieke,Bushby Kate,Furlong Pat,Goemans Nathalie,De Luca Annamaria,Mayhew Anna,McDonald Craig,Mercuri Eugenio,Muntoni Francesco,Pohlschmidt Marita,Verschuuren Jan,Voit Thomas,Vroom Elizabeth,Wells Dominic J.,Straub Volker

Funder

Muscular Dystrophy Campaign

Parent Project Muscular Dystrophy

United Parent Projects Muscular Dystrophy

AFM Telethon

BMBS COST Action BM1207

Publisher

Elsevier BV

Subject

Genetics(clinical),Clinical Neurology,Neurology,Pediatrics, Perinatology, and Child Health

Reference46 articles.

1. Genotype/phenotype correlations in Duchenne/Becker dystrophy;Hoffman;Mol Cell Biol Hum Dis Ser,1993

2. Enhancing translation: guidelines for standard pre-clinical experiments in mdx mice;Willmann;Neuromuscul Disord,2012

3. Developing standard procedures for murine and canine efficacy studies of DMD therapeutics: report of two expert workshops on “Pre-clinical testing for Duchenne dystrophy”: Washington DC, October 27th–28th 2007 and Zurich, June 30th–July 1st 2008;Nagaraju;Neuromuscul Disord,2009

4. Mammalian animal models for Duchenne muscular dystrophy;Willmann;Neuromuscul Disord,2009

5. The TREAT-NMD Duchenne muscular dystrophy registries: conception, design, and utilization by industry and academia;Bladen;Hum Mutat,2013

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