Tamoxifen in children with Duchenne muscular dystrophy
Author:
Publisher
Elsevier BV
Subject
Neurology (clinical)
Reference10 articles.
1. Emerging therapies for Duchenne muscular dystrophy;Markati;Lancet Neurol,2022
2. Assessment of systemic delivery of rAAVrh74.MHCK7.micro-dystrophin in children with Duchenne muscular dystrophy: a nonrandomized controlled trial;Mendell;JAMA Neurol,2020
3. A state-of-the-art review of tamoxifen as a potential therapeutic for Duchenne muscular dystrophy;Botti;Front Pharmacol,2022
4. Safety and clinical outcome of tamoxifen in Duchenne muscular dystrophy;Tsabari;Neuromuscul Disord,2021
5. Safety and efficacy of tamoxifen in Duchenne muscular dystrophy (TAMDMD): a multicentre, randomised, doucle-blind, placebo-controlled, phase 3 trial;Henzi;Lancet Neurol,2023
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