Epigenetic and neurological effects and safety of high-dose nicotinamide in patients with Friedreich's ataxia: an exploratory, open-label, dose-escalation study-Reference-Cited by-同舟云学术

Epigenetic and neurological effects and safety of high-dose nicotinamide in patients with Friedreich's ataxia: an exploratory, open-label, dose-escalation study

Published:2014-08 Issue:9942 Volume:384 Page:504-513
ISSN:0140-6736
Container-title:The Lancet
language:en
Short-container-title:The Lancet

Author:

Libri Vincenzo,Yandim Cihangir,Athanasopoulos Stavros,Loyse Naomi,Natisvili Theona,Law Pui Pik,Chan Ping Kei,Mohammad Tariq,Mauri Marta,Tam Kin Tung,Leiper James,Piper Sophie,Ramesh Aravind,Parkinson Michael H,Huson Les,Giunti Paola,Festenstein Richard

Publisher

Elsevier BV

Subject

General Medicine

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4. Friedreich's ataxia: autosomal recessive disease caused by an intronic GAA triplet repeat expansion;Campuzano;Science,1996

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