Repeated nebulisation of non-viral CFTR gene therapy in patients with cystic fibrosis: a randomised, double-blind, placebo-controlled, phase 2b trial

Author:

Alton Eric W F W,Armstrong David K,Ashby Deborah,Bayfield Katie J,Bilton Diana,Bloomfield Emily V,Boyd A Christopher,Brand June,Buchan Ruaridh,Calcedo Roberto,Carvelli Paula,Chan Mario,Cheng Seng H,Collie D David S,Cunningham Steve,Davidson Heather E,Davies Gwyneth,Davies Jane C,Davies Lee A,Dewar Maria H,Doherty Ann,Donovan Jackie,Dwyer Natalie S,Elgmati Hala I,Featherstone Rosanna F,Gavino Jemyr,Gea-Sorli Sabrina,Geddes Duncan M,Gibson James S R,Gill Deborah R,Greening Andrew P,Griesenbach Uta,Hansell David M,Harman Katharine,Higgins Tracy E,Hodges Samantha L,Hyde Stephen C,Hyndman Laura,Innes J Alastair,Jacob Joseph,Jones Nancy,Keogh Brian F,Limberis Maria P,Lloyd-Evans Paul,Maclean Alan W,Manvell Michelle C,McCormick Dominique,McGovern Michael,McLachlan Gerry,Meng Cuixiang,Montero M Angeles,Milligan Hazel,Moyce Laura J,Murray Gordon D,Nicholson Andrew G,Osadolor Tina,Parra-Leiton Javier,Porteous David J,Pringle Ian A,Punch Emma K,Pytel Kamila M,Quittner Alexandra L,Rivellini Gina,Saunders Clare J,Scheule Ronald K,Sheard Sarah,Simmonds Nicholas J,Smith Keith,Smith Stephen N,Soussi Najwa,Soussi Samia,Spearing Emma J,Stevenson Barbara J,Sumner-Jones Stephanie G,Turkkila Minna,Ureta Rosa P,Waller Michael D,Wasowicz Marguerite Y,Wilson James M,Wolstenholme-Hogg Paul

Publisher

Elsevier BV

Subject

Pulmonary and Respiratory Medicine

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