Synthesis of (3 S ,4 S ,5 S )-trihydroxylpiperidine derivatives as enzyme stabilizers to improve therapeutic enzyme activity in Fabry patient cell lines-Reference-Cited by-同舟云学术

Synthesis of (3 S ,4 S ,5 S )-trihydroxylpiperidine derivatives as enzyme stabilizers to improve therapeutic enzyme activity in Fabry patient cell lines

Published:2018-01 Issue: Volume:144 Page:626-634
ISSN:0223-5234
Container-title:European Journal of Medicinal Chemistry
language:en
Short-container-title:European Journal of Medicinal Chemistry

Author:

Li Huang-Yi,Lee Jay-Der,Chen Chiao-Wen,Sun Ying-Chieh,Cheng Wei-Chieh

Funder

Ministry of Science and Technology (MOST)

Academia Sinica

Taiwan Foundation

Publisher

Elsevier BV

Subject

Organic Chemistry,Drug Discovery,Pharmacology,General Medicine

Reference23 articles.

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2. Molecular basis of 1-deoxygalactonojirimycin arylthiourea binding to human α-galactosidase A: pharmacological chaperoning efficacy on Fabry disease mutants;Yu;ACS Chem. Biol.,2014

3. Newborn screening for Fabry disease by measuring GLA activity using tandem mass spectrometry;Dajnoki;Clin. Chim. Acta,2010

4. Enzyme replacement therapy in Fabry disease: a randomized controlled trial;Schiffmann;JAMA,2001

5. Safety and efficacy of recombinant human alpha-galactosidase A replacement therapy in Fabry's disease;Eng;N. Engl. J. Med.,2001

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