Bioevaluation of sixteen ADMDP stereoisomers toward alpha-galactosidase A: Development of a new pharmacological chaperone for the treatment of Fabry disease and potential enhancement of enzyme replacement therapy efficiency-Reference-Cited by-同舟云学术

Bioevaluation of sixteen ADMDP stereoisomers toward alpha-galactosidase A: Development of a new pharmacological chaperone for the treatment of Fabry disease and potential enhancement of enzyme replacement therapy efficiency

Published:2016-11 Issue: Volume:123 Page:14-20
ISSN:0223-5234
Container-title:European Journal of Medicinal Chemistry
language:en
Short-container-title:European Journal of Medicinal Chemistry

Author:

Cheng Wei-Chieh,Wang Jen-Hon,Li Huang-Yi,Lu Sheng-Jhih,Hu Jia-Ming,Yun Wen-Yi,Chiu Cheng-Hsin,Yang Wen-Bin,Chien Yin-Hsiu,Hwu Wuh-Liang

Funder

Academia Sinica

Ministry of Science and Technology

Taiwan Foundation

Publisher

Elsevier BV

Subject

Organic Chemistry,Drug Discovery,Pharmacology,General Medicine

Reference28 articles.

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2. Molecular basis of 1-deoxygalactonojirimycin arylthiourea binding to human α-galactosidase A: pharmacological chaperoning efficacy on Fabry disease mutants;Yu;ACS Chem. Biol.,2014

3. Newborn screening for Fabry disease by measuring GLA activity using tandem mass spectrometry;Dajnoki;Clin. Chim. Acta,2010

4. Safety and efficacy of recombinant human α-galactosidase A replacement therapy in Fabry's disease;Eng;N. Engl. J. Med.,2001

5. Enzyme replacement therapy in Fabry disease: a randomized controlled trial;Schiffmann;JAMA,2001

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