Miglustat therapy in type 1 Gaucher disease: Clinical and safety outcomes in a multicenter retrospective cohort study-Reference-Cited by-同舟云学术

Miglustat therapy in type 1 Gaucher disease: Clinical and safety outcomes in a multicenter retrospective cohort study

Published:2013-08 Issue:2 Volume:51 Page:116-124
ISSN:1079-9796
Container-title:Blood Cells, Molecules, and Diseases
language:en
Short-container-title:Blood Cells, Molecules, and Diseases

Author:

Kuter David J.,Mehta Atul,Hollak Carla E.M.,Giraldo Pilar,Hughes Derralynn,Belmatoug Nadia,Brand Monika,Muller Audrey,Schaaf Berthold,Giorgino Ruben,Zimran Ari

Publisher

Elsevier BV

Subject

Cell Biology,Hematology,Molecular Biology,Molecular Medicine

Reference26 articles.

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4. Sustained therapeutic effects of oral miglustat (Zavesca, N-butyldeoxynojirimycin, OGT 918) in type I Gaucher disease;Elstein;J. Inherit. Metab. Dis.,2004

5. Novel oral treatment of Gaucher's disease with N-butyldeoxynojirimycin (OGT 918) to decrease substrate biosynthesis;Cox;Lancet,2000

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