Early access experience with VPRIV®: Recommendations for ‘core data’ collection-Reference-Cited by-同舟云学术

Early access experience with VPRIV®: Recommendations for ‘core data’ collection

Published:2011-08 Issue:2 Volume:47 Page:140-142
ISSN:1079-9796
Container-title:Blood Cells, Molecules, and Diseases
language:en
Short-container-title:Blood Cells, Molecules, and Diseases

Author:

Hughes Derralynn A.,Al-Sayed Moeen,Belmatoug Nadia,Bodamer Olaf,Böttcher Tobias,Cappellini Maria,Cohen Ian J.,Eagleton Terence,Elstein Deborah,Giraldo Pilar,Jones Simon,Kaplinsky Chaim,Lund Allan,Machaczka Maciej,Mengel Eugen,Pastores Gregory M.,Rosenbaum Hanna,Sjo Malvin,Tiling Nikolaus,Tsaftaridis Panagiotis,Zimran Ari,Weinreb Neal

Publisher

Elsevier BV

Subject

Cell Biology,Hematology,Molecular Biology,Molecular Medicine

Reference8 articles.

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2. Velaglucerase alfa, a human recombinant glucocerebrosidase enzyme replacement therapy for type 1 Gaucher disease;Pastores;Curr. Opin. Investig. Drugs,2010

3. Early achievement and maintenance of the therapeutic goals using velaglucerase alfa in type 1 Gaucher disease;Elstein;Blood Cells Mol. Dis.,2011

4. Guidelines for the restart of imiglucerase in patients with Gaucher disease: recommendations from the European Working Group on Gaucher disease;Hollak;Blood Cells Mol. Dis.,2010

5. Recommendations for treating patients with Gaucher disease with emerging enzyme products;Cox;Blood Cells Mol. Dis.,2010

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1. Treatment patterns from 647 patients with Gaucher disease: An analysis from the Gaucher Outcome Survey;Blood Cells, Molecules, and Diseases;2018-02

2. Atypical cytomorphology of Gaucher cells is frequently seen in bone marrow smears from untreated patients with Gaucher disease type 1;Folia Histochemica et Cytobiologica;2015-04-14

3. Patients with type 1 Gaucher disease in South Florida, USA: demographics, genotypes, disease severity and treatment outcomes;Orphanet Journal of Rare Diseases;2014-03-31

4. Safety and efficacy of velaglucerase alfa replacement therapy for patients with type 1 Gaucher disease;Expert Review of Endocrinology & Metabolism;2013-07