Update of treatment for mucopolysaccharidosis type III (sanfilippo syndrome)
Author:
Funder
MPS
III
Research Foundation of Beijing Friendship Hospital
Capital Medical University
Publisher
Elsevier BV
Subject
Pharmacology
Reference91 articles.
1. Sanfilippo syndrome: overall review;Andrade;Pediatr. Int.,2015
2. Clearance of heparan sulfate and attenuation of CNS pathology by intracerebroventricular BMN 250 in Sanfilippo type B mice;Aoyagi-Scharber;Mol Ther Methods Clin Dev,2017
3. Neuroinflammatory and oxidative stress phenomena in MPS IIIA mouse model: the positive effect of long-term aspirin treatment;Arfi;Mol. Genet. Metabol.,2011
4. Storage correction in cells of patients suffering from mucopolysaccharidoses types IIIA and VII after treatment with genistein and other isoflavones;Arfi;J. Inherit. Metab. Dis.,2010
5. Early neurodegeneration progresses independently of microglial activation by heparan sulfate in the brain of mucopolysaccharidosis IIIB mice;Ausseil;PLoS One,2008
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