Pharmacokinetics and clinical efficacy of 6′-sialyllactose in patients with GNE myopathy: Randomized pilot trial
Author:
Funder
Ministry of SMEs and Startups
Publisher
Elsevier BV
Subject
Pharmacology,General Medicine
Reference19 articles.
1. Reduction of UDP-N-acetylglucosamine 2-epimerase/N-acetylmannosamine kinase activity and sialylation in distal myopathy with rimmed vacuoles;Noguchi;J. Biol. Chem.,2004
2. Prophylactic treatment with sialic acid metabolites precludes the development of the myopathic phenotype in the DMRV-hIBM mouse model;Malicdan;Nat. Med.,2009
3. Aceneuramic acid extended release administration maintains upper limb muscle strength in a 48-week study of subjects with GNE myopathy: results from a phase 2, randomized, controlled study;Argov;J. Neuromuscul. Dis.,2016
4. A phase 3 randomized study evaluating sialic acid extended-release for GNE myopathy;Lochmüller;Neurology,2019
5. Safety, pharmacokinetics and sialic acid production after oral administration of N-acetylmannosamine (ManNAc) to subjects with GNE myopathy;Xu;Mol. Genet. Metab.,2017
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1. 6′-Sialyllactose Alleviates Muscle Fatigue through Reduced Blood Lactate Level after Treadmill Exercise in Mice;Nutrients;2024-09-03
2. Induced Muscle and Liver Absence of Gne in Postnatal Mice Does Not Result in Structural or Functional Muscle Impairment;Journal of Neuromuscular Diseases;2024-09-03
3. 6′-Sialyllactose Enhances Exercise Performance via Increased Muscle Mass and Strength;Nutrients;2024-08-07
4. Recessive GNE Mutations in Korean Nonaka Distal Myopathy Patients with or without Peripheral Neuropathy;Genes;2024-04-11
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