Repurposing pentamidine using hyaluronic acid-based nanocarriers for skeletal muscle treatment in myotonic dystrophy

Author:

Repellin Mathieu,Carton Flavia,Boschi Federico,Galiè Mirco,Perduca Massimiliano,Calderan Laura,Jacquier Arnaud,Carras Julien,Schaeffer Laurent,Briançon Stéphanie,Lollo Giovanna,Malatesta Manuela

Funder

Università degli Studi di Verona

Horizon 2020

H2020 Marie Skłodowska-Curie Actions

Université de Lyon

Publisher

Elsevier BV

Subject

Pharmaceutical Science,General Materials Science,Biomedical Engineering,Molecular Medicine,Medicine (miscellaneous),Bioengineering

Reference57 articles.

1. Myotonic dystrophy;Thornton;Neurol. Clin.,2014

2. Meola, G. Clinical Aspects, Molecular Pathomechanisms and Management of Myotonic Dystrophies. Clinical aspects 12.

3. Molecular basis of myotonic dystrophy: expansion of a trinucleotide (CTG) repeat at the 3’ end of a transcript encoding a protein kinase family member;Brook;Cell,1992

4. Pathogenic mechanisms of myotonic dystrophy;Lee;Biochem. Soc. Trans.,2009

5. Disruption of splicing regulated by a CUG-binding protein in myotonic dystrophy;Philips;Science,1998

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