Gene therapy strategies for rare monogenic disorders with nuclear or mitochondrial gene mutations
Author:
Publisher
Elsevier BV
Subject
Mechanics of Materials,Biomaterials,Biophysics,Ceramics and Composites,Bioengineering
Reference162 articles.
1. A look to future directions in gene therapy research for monogenic diseases,;Porteus;PLoS Genet.,2006
2. Improvement and decline in vision with gene therapy in childhood blindness, N. Engl;Jacobson;J. Med.,2015
3. Global, regional, and national burden of neurological disorders during 1990–2015: a systematic analysis for the Global Burden of Disease Study 2015
4. A revised airway epithelial hierarchy includes CFTR-expressing ionocytes,;Montoro;Nature,2018
5. Sickle cell disease;Kato;Nat. Rev. Dis. Primers,2018
Cited by 14 articles. 订阅此论文施引文献 订阅此论文施引文献,注册后可以免费订阅5篇论文的施引文献,订阅后可以查看论文全部施引文献
1. Biotechnology Advances in Disease Treatment;International Encyclopedia of Public Health;2025
2. Innovative genetic scissor strategies and their applications in cancer treatment and prevention: CRISPR modules and challenges;International Journal of Biological Macromolecules;2024-11
3. DPA-Zn enables targeting and bypassing endosomal trapping delivery of a genome-editing system into cancer cells via phosphatidylserine-mediated endocytic pathway;Chemical Engineering Journal;2024-10
4. Mitochondrial endogenous substance transport-inspired nanomaterials for mitochondria-targeted gene delivery;Advanced Drug Delivery Reviews;2024-08
5. Nanoengineered mitochondria enable ocular mitochondrial disease therapy via the replacement of dysfunctional mitochondria;Acta Pharmaceutica Sinica B;2024-08
1.学者识别学者识别
2.学术分析学术分析
3.人才评估人才评估
"同舟云学术"是以全球学者为主线,采集、加工和组织学术论文而形成的新型学术文献查询和分析系统,可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容,当前同舟云学术共收录了国内外主流学术期刊6万余种,收集的期刊论文及会议论文总量共计约1.5亿篇,并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询!咨询电话:010-8811{复制后删除}0370
www.globalauthorid.com
TOP
Copyright © 2019-2024 北京同舟云网络信息技术有限公司 京公网安备11010802033243号 京ICP备18003416号-3