Three‐Year Safety Results of SAR422459 (EIAV‐ABCA4) Gene Therapy in Patients With ABCA4‐Associated Stargardt Disease: An Open‐Label Dose‐Escalation Phase I/IIa Clinical Trial, Cohorts 1‐5-Reference-Cited by-同舟云学术

Three‐Year Safety Results of SAR422459 (EIAV‐ABCA4) Gene Therapy in Patients With ABCA4‐Associated Stargardt Disease: An Open‐Label Dose‐Escalation Phase I/IIa Clinical Trial, Cohorts 1‐5

Published:2022-08 Issue: Volume:240 Page:285-301
ISSN:0002-9394
Container-title:American Journal of Ophthalmology
language:en
Short-container-title:American Journal of Ophthalmology

Author:

Parker Maria A.,Erker Laura R.,Audo Isabelle^ORCID,Choi Dongseok^ORCID,Mohand-Said Saddek,Sestakauskas Kastytis^ORCID,Benoit Patrick^ORCID,Appelqvist Terence,Krahmer Melissa,Ségaut-Prévost Caroline^ORCID,Lujan Brandon J.^ORCID,Faridi Ambar,Chegarnov Elvira N.^ORCID,Steinkamp Peter N.,Ku Cristy,da Palma Mariana Matioli^ORCID,Barale Pierre-Olivier,Ayelo-Scheer Sarah,Lauer Andreas^ORCID,Stout Tim,Wilson David J.,Weleber Richard G.,Pennesi Mark E.,Sahel José Alain^ORCID,Yang Paul^ORCID

Funder

National Institutes of Health

Research to Prevent Blindness

Publisher

Elsevier BV

Subject

Ophthalmology

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