Safety of Lenadogene Nolparvovec Gene Therapy Over 5 Years in 189 Patients With Leber Hereditary Optic Neuropathy-Reference-Cited by-同舟云学术

Safety of Lenadogene Nolparvovec Gene Therapy Over 5 Years in 189 Patients With Leber Hereditary Optic Neuropathy

Published:2023-05 Issue: Volume:249 Page:108-125
ISSN:0002-9394
Container-title:American Journal of Ophthalmology
language:en
Short-container-title:American Journal of Ophthalmology

Author:

VIGNAL-CLERMONT CATHERINE^ORCID,YU-WAI-MAN PATRICK^ORCID,NEWMAN NANCY J.,CARELLI VALERIO^ORCID,MOSTER MARK L.^ORCID,BIOUSSE VALERIE,SUBRAMANIAN PREM S.^ORCID,WANG AN-GUOR,DONAHUE SEAN P.,LEROY BART P.,SADUN ALFREDO A.,KLOPSTOCK THOMAS^ORCID,SERGOTT ROBERT C.,REBOLLEDA FERNANDEZ GEMA,CHWALISZ BART K.,BANIK RUDRANI,TAIEL MAGALI^ORCID,ROUX MICHEL,SAHEL JOSÉ-ALAIN

Publisher

Elsevier BV

Subject

Ophthalmology

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5. Visual outcomes in Leber hereditary optic neuropathy patients with the m.11778G>A (MTND4) mitochondrial DNA mutation;Newman;J Neuroophthalmol,2020

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