First-in-Human Gene Therapy Trial of AAV8-hCARp.hCNGB3 in Adults and Children With CNGB3-associated Achromatopsia-Reference-Cited by-同舟云学术

First-in-Human Gene Therapy Trial of AAV8-hCARp.hCNGB3 in Adults and Children With CNGB3-associated Achromatopsia

Published:2023-09 Issue: Volume:253 Page:243-251
ISSN:0002-9394
Container-title:American Journal of Ophthalmology
language:en
Short-container-title:American Journal of Ophthalmology

Author:

Michaelides Michel,Hirji Nashila,Wong Sui Chien,Besirli Cagri G.^ORCID,Zaman Serena^ORCID,Kumaran Neruban^ORCID,Georgiadis Anastasios,Smith Alexander J.,Ripamonti Caterina,Gottlob Irene,Robson Anthony G.,Thiadens Alberta,Henderson Robert H.,Fleck Penny,Anglade Eddy,Dong Xiangwen,Capuano George,Lu Wentao,Berry Pamela^ORCID,Kane Thomas,Naylor Stuart,Georgiou Michalis,Kalitzeos Angelos^ORCID,Ali Robin R.,Forbes Alexandria,Bainbridge James

Publisher

Elsevier BV

Subject

Ophthalmology

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