Long-Term Structural Outcomes of Late-Stage RPE65 Gene Therapy-Reference-Cited by-同舟云学术

Long-Term Structural Outcomes of Late-Stage RPE65 Gene Therapy

Published:2020-01 Issue:1 Volume:28 Page:266-278
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Gardiner Kristin L.,Cideciyan Artur V.,Swider Malgorzata,Dufour Valérie L.,Sumaroka Alexander,Komáromy András M.,Hauswirth William W.,Iwabe Simone,Jacobson Samuel G.,Beltran William A.,Aguirre Gustavo D.

Funder

National Eye Institute

Foundation Fighting Blindness

Van Sloun Fund for Canine Genetic Research

BrightFocus Foundation

Vice Provost for Research at the University of Pennsylvania

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference54 articles.

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2. Gene therapy restores vision in a canine model of childhood blindness;Acland;Nat. Genet.,2001

3. In utero gene therapy rescues vision in a murine model of congenital blindness;Dejneka;Mol. Ther.,2004

4. Long-term restoration of rod and cone vision by single dose rAAV-mediated gene transfer to the retina in a canine model of childhood blindness;Acland;Mol. Ther.,2005

5. Effect of gene therapy on visual function in Leber’s congenital amaurosis;Bainbridge;N. Engl. J. Med.,2008

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