Paired nicking-mediated COL17A1 reframing for junctional epidermolysis bullosa-Reference-Cited by-同舟云学术

Paired nicking-mediated COL17A1 reframing for junctional epidermolysis bullosa

Published:2022-08 Issue:8 Volume:30 Page:2680-2692
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Bischof Johannes^ORCID,March Oliver Patrick,Liemberger Bernadette,Haas Simone Alexandra,Hainzl Stefan,Petković Igor,Leb-Reichl Victoria,Illmer Julia,Korotchenko Evgeniia,Klausegger Alfred,Hoog Anna,Binder Heide-Marie,Garcia Marta,Duarte Blanca,Strunk Dirk,Larcher Fernando,Reichelt Julia,Guttmann-Gruber Christina,Wally Verena,Hofbauer Josefina Piñón,Bauer Johann Wolfgang,Cathomen Toni,Kocher Thomas,Koller Ulrich

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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