Rescue of hearing by adenine base editing in a humanized mouse model of Usher syndrome type 1F-Reference-Cited by-同舟云学术

Rescue of hearing by adenine base editing in a humanized mouse model of Usher syndrome type 1F

Published:2023-08 Issue:8 Volume:31 Page:2439-2453
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Peters Cole W.,Hanlon Killian S.,Ivanchenko Maryna V.,Zinn Eric,Linarte Elizabeth F.,Li Yaqiao,Levy Jonathan M.,Liu David R.,Kleinstiver Benjamin P.,Indzhykulian Artur A.,Corey David P.^ORCID

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference54 articles.

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2. Towards gene therapy for deafness;Di Domenico;J. Cel. Physiol.,2011

3. Profound deafness in childhood;Kral;N. Engl. J. Med.,2010

4. Global hearing health care: new findings and perspectives;Wilson;Lancet,2017

5. Hereditary Hearing Loss and Deafness Overview;Shearer,1993

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