Gene Therapy Corrects Brain and Behavioral Pathologies in CLN6-Batten Disease-Reference-Cited by-同舟云学术

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Gene Therapy Corrects Brain and Behavioral Pathologies in CLN6-Batten Disease

Published:2019-10 Issue:10 Volume:27 Page:1836-1847
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Cain Jacob T.,Likhite Shibi,White Katherine A.,Timm Derek J.,Davis Samantha S.,Johnson Tyler B.,Dennys-Rivers Cassandra N.,Rinaldi Federica,Motti Dario,Corcoran Sarah,Morales Pablo,Pierson Christopher,Hughes Stephanie M.,Lee Stella Y.,Kaspar Brian K.,Meyer Kathrin^ORCID,Weimer Jill M.

Funder

Charlotte and Gwenyth Gray Foundation

NIH

Sanford Research Imaging Core

Sanford Research Center for Pediatric Research

Sanford Research Molecular Pathology Core

Sanford Research Center for Cancer Biology

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference45 articles.

1. Genetics of the neuronal ceroid lipofuscinoses (Batten disease);Mole;Biochim. Biophys. Acta,2015

2. Neuronal ceroid-lipofuscinoses in childhood;Santavuori;Brain Dev.,1988

3. Batten disease: past, present, and future;Rider;Am. J. Med. Genet. Suppl.,1988

4. Mitochondrial ATP synthase subunit c storage in the ceroid-lipofuscinoses (Batten disease);Palmer;Am. J. Med. Genet.,1992

5. Variant late infantile ceroid lipofuscinoses associated with novel mutations in CLN6;Cannelli;Biochem. Biophys. Res. Commun.,2009

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