CRISPR-Induced Deletion with SaCas9 Restores Dystrophin Expression in Dystrophic Models In Vitro and In Vivo-Reference-Cited by-同舟云学术

CRISPR-Induced Deletion with SaCas9 Restores Dystrophin Expression in Dystrophic Models In Vitro and In Vivo

Published:2018-11 Issue:11 Volume:26 Page:2604-2616
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Duchêne Benjamin L.,Cherif Khadija,Iyombe-Engembe Jean-Paul,Guyon Antoine,Rousseau Joel,Ouellet Dominique L.,Barbeau Xavier,Lague Patrick,Tremblay Jacques P.

Funder

Canadian Institute of Health Research

Foundation for Cell and Gene Therapy

The Cell Network

MITACs

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference61 articles.

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