CRISPR/Cas9-Mediated Gene Correction in Newborn Rabbits with Hereditary Tyrosinemia Type I-Reference-Cited by-同舟云学术

CRISPR/Cas9-Mediated Gene Correction in Newborn Rabbits with Hereditary Tyrosinemia Type I

Published:2021-03 Issue:3 Volume:29 Page:1001-1015
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Li Nan,Gou Shixue,Wang Jiaowei,Zhang Quanjun,Huang Xingyun,Xie Jingke,Li Li,Jin Qin,Ouyang Zhen,Chen Fangbing,Ge Weikai,Shi Hui,Liang Yanhui,Zhuang Zhenpeng,Zhao Xiaozhu,Lian Meng,Ye Yinghua,Quan Longquan,Wu Han,Lai Liangxue,Wang Kepin

Funder

Guangzhou Municipal Science and Technology Project

National Natural Science Foundation of China

National Key Research and Development Program of China

China Postdoctoral Science Foundation

Science and Technology Planning Project of Guangdong Province

Youth Innovation Promotion Association of the Chinese Academy of Sciences

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference33 articles.

1. Treatment of hereditary tyrosinaemia type I by inhibition of 4-hydroxyphenylpyruvate dioxygenase;Lindstedt;Lancet,1992

2. Mutations in the fumarylacetoacetate hydrolase gene causing hereditary tyrosinemia type I: overview;St-Louis;Hum. Mutat.,1997

3. Visceral pathology of hereditary tyrosinemia type I;Russo;Am. J. Hum. Genet.,1990

4. Cross-sectional study of 168 patients with hepatorenal tyrosinaemia and implications for clinical practice;Mayorandan;Orphanet J. Rare Dis.,2014

5. Evolution of indications and results of liver transplantation in Europe. A report from the European Liver Transplant Registry (ELTR);Adam;J. Hepatol.,2012

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