Third-generation lentiviral gene therapy rescues function in a mouse model of Usher 1B
Author:
Publisher
Elsevier BV
Subject
Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine
Reference42 articles.
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3. The autosomal recessive isolated deafness, DFNB2, and the Usher 1B syndrome are allelic defects of the myosin-VIIA gene;Weil;Nat. Genet.,1997
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