Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model-Reference-Cited by-同舟云学术

Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model

Published:2021-11 Issue: Volume: Page:
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Bersani Margherita,Rizzuti Mafalda,Pagliari Elisa,Garbellini Manuela,Saccomanno Domenica,Moulton Hong M.,Bresolin Nereo,Comi Giacomo P.,Corti Stefania,Nizzardo Monica

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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