A Phase 2/3 Trial of Pabinafusp Alfa, IDS Fused with Anti-Human Transferrin Receptor Antibody, Targeting Neurodegeneration in MPS-II-Reference-Cited by-同舟云学术

A Phase 2/3 Trial of Pabinafusp Alfa, IDS Fused with Anti-Human Transferrin Receptor Antibody, Targeting Neurodegeneration in MPS-II

Published:2021-02 Issue:2 Volume:29 Page:671-679
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Okuyama Torayuki,Eto Yoshikatsu,Sakai Norio,Nakamura Kimitoshi,Yamamoto Tatsuyoshi,Yamaoka Mariko,Ikeda Toshiaki,So Sairei,Tanizawa Kazunori,Sonoda Hiroyuki,Sato Yuji^ORCID

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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