High Levels of Persistent Expression of α1-Antitrypsin Mediated by the Nonhuman Primate Serotype rh.10 Adeno-associated Virus Despite Preexisting Immunity to Common Human Adeno-associated Viruses-Reference-Cited by-同舟云学术

High Levels of Persistent Expression of α1-Antitrypsin Mediated by the Nonhuman Primate Serotype rh.10 Adeno-associated Virus Despite Preexisting Immunity to Common Human Adeno-associated Viruses

Published:2006-01 Issue:1 Volume:13 Page:67-76
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

De Bishnu P.,Heguy Adriana,Hackett Neil R.,Ferris Barbara,Leopold Philip L.,Lee John,Pierre Lorraine,Gao Guangping,Wilson James M.,Crystal Ronald G.

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference51 articles.

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3. Alpha 1-antitrypsin deficiency, emphysema, and liver disease: genetic basis and strategies for therapy;Crystal;J. Clin. Invest.,1990

4. α1-Antitrypsin deficiency;Cox Wilson,1995

5. Human plasma proteinase inhibitors;Travis;Annu. Rev. Biochem.,1983

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