Cell type-selective targeted delivery of a recombinant lysosomal enzyme for enzyme therapies-Reference-Cited by-同舟云学术

Cell type-selective targeted delivery of a recombinant lysosomal enzyme for enzyme therapies

Published:2021-12 Issue:12 Volume:29 Page:3512-3524
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Baik Andrew D.^ORCID,Calafati Philip^ORCID,Zhang Xiaoli^ORCID,Aaron Nina A.,Mehra Antonia^ORCID,Moller-Tank Sven^ORCID,Miloscio Lawrence,Praggastis Maria,Giovannone Nicholas,Pan Cheryl^ORCID,Tang Yajun,Bridges Susannah,Mujica Alejo,Barbounis Peter,Yanolatos Jean,Gale Nicholas^ORCID,Li Ning^ORCID,Kyratsous Christos A.^ORCID,Schoenherr Christopher J.^ORCID,Murphy Andrew J.^ORCID,Economides Aris N.^ORCID,Cygnar Katherine D.^ORCID

Funder

Regeneron Pharmaceuticals

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

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