Gene Therapy for Cystic Fibrosis: Lessons Learned and Paths Forward-Reference-Cited by-同舟云学术

登录注册会员服务联系我们

Gene Therapy for Cystic Fibrosis: Lessons Learned and Paths Forward

Published:2021-02 Issue:2 Volume:29 Page:428-430
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Choi Soon H.,Engelhardt John F.

Funder

National Heart, Lung, and Blood Institute

National Institute of Diabetes and Digestive and Kidney Diseases

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference15 articles.

1. Administration of an adenovirus containing the human CFTR cDNA to the respiratory tract of individuals with cystic fibrosis;Crystal;Nat. Genet.,1994

2. Efficient and persistent gene transfer of AAV-CFTR in maxillary sinus;Wagner;Lancet,1998

3. Repeated aerosolized AAV-CFTR for treatment of cystic fibrosis: a randomized placebo-controlled phase 2B trial;Moss;Hum. Gene Ther.,2007

4. Endosomal processing limits gene transfer to polarized airway epithelia by adeno-associated virus;Duan;J. Clin. Invest.,2000

5. Ubiquitination of both adeno-associated virus type 2 and 5 capsid proteins affects the transduction efficiency of recombinant vectors;Yan;J. Virol.,2002

Cited by 9 articles. 订阅此论文施引文献订阅此论文施引文献，注册后可以免费订阅5篇论文的施引文献，订阅后可以查看论文全部施引文献

1. Inhalation of SP-101 Followed by Inhaled Doxorubicin Results in Robust and Durable hCFTRΔR Transgene Expression in the Airways of Wild-Type and Cystic Fibrosis Ferrets;Human Gene Therapy;2024-09-04

2. Evaluation of anti-vector immune responses to adenovirus-mediated lung gene therapy and modulation by αCD20;Molecular Therapy - Methods & Clinical Development;2024-09

3. Poly(vinyl alcohol) (PVA) for gene delivery: a systematic review;Journal of Drug Delivery Science and Technology;2024-09

4. SP-101, A Novel Adeno-Associated Virus Gene Therapy for the Treatment of Cystic Fibrosis, Mediates Functional Correction of Primary Human Airway Epithelia From Donors with Cystic Fibrosis;Human Gene Therapy;2024-08-29

5. Protospacer modification improves base editing of a canonical splice site variant and recovery of CFTR function in human airway epithelial cells;Molecular Therapy - Nucleic Acids;2023-09

同舟云学术

1.学者识别学者识别

2.学术分析学术分析

3.人才评估人才评估

"同舟云学术"是以全球学者为主线，采集、加工和组织学术论文而形成的新型学术文献查询和分析系统，可以对全球学者进行文献检索和人才价值评估。用户可以通过关注某些学科领域的顶尖人物而持续追踪该领域的学科进展和研究前沿。经过近期的数据扩容，当前同舟云学术共收录了国内外主流学术期刊6万余种，收集的期刊论文及会议论文总量共计约1.5亿篇，并以每天添加12000余篇中外论文的速度递增。我们也可以为用户提供个性化、定制化的学者数据。欢迎来电咨询！咨询电话：010-8811{复制后删除}0370

www.globalauthorid.com

TOP

Copyright © 2019-2024 北京同舟云网络信息技术有限公司
京公网安备11010802033243号京ICP备18003416号-3