Correction of Three Prominent Mutations in Mouse and Human Models of Duchenne Muscular Dystrophy by Single-Cut Genome Editing-Reference-Cited by-同舟云学术

Correction of Three Prominent Mutations in Mouse and Human Models of Duchenne Muscular Dystrophy by Single-Cut Genome Editing

Published:2020-09 Issue:9 Volume:28 Page:2044-2055
ISSN:1525-0016
Container-title:Molecular Therapy
language:en
Short-container-title:Molecular Therapy

Author:

Min Yi-Li,Chemello Francesco,Li Hui,Rodriguez-Caycedo Cristina,Sanchez-Ortiz Efrain,Mireault Alex A.,McAnally John R.,Shelton John M.,Zhang Yu,Bassel-Duby Rhonda,Olson Eric N.

Funder

Foundation for the National Institutes of Health

Welch Foundation

Publisher

Elsevier BV

Subject

Drug Discovery,Pharmacology,Genetics,Molecular Biology,Molecular Medicine

Reference48 articles.

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3. Association of dystrophin and an integral membrane glycoprotein;Campbell;Nature,1989

4. The TREAT-NMD DMD Global Database: analysis of more than 7,000 Duchenne muscular dystrophy mutations;Bladen;Hum. Mutat.,2015

5. Entries in the Leiden Duchenne muscular dystrophy mutation database: an overview of mutation types and paradoxical cases that confirm the reading-frame rule;Aartsma-Rus;Muscle Nerve,2006

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